Barth Syndrome - Search Videos

Americans With Rare Barth Syndrome Losing Hope in FDA

Americans With Rare Barth Syndrome Losing Hope in FDA

16.6K views3 days ago

YouTubeInside Edition

Chicago-area family fights FDA over approval of drug to treat rare genetic disease

Chicago-area family fights FDA over approval of drug to treat rare gene…

385 views5 days ago

YouTubeABC 7 Chicago

Chicago-area family fights FDA over rare genetic disorder treatment

Chicago-area family fights FDA over rare genetic disorder treatment

Microsoft NewsABC 7 Chicago

Stealth BioTherapeutics Resubmits NDA for Elamipretide to Treat Barth Syndrome

Stealth BioTherapeutics Resubmits NDA for Elamipretide to Treat Bart…

YouTubeNowCulture

FDA Accelerates Review of Ultra-Rare Barth Syndrome Drug – What This Means for Patients

FDA Accelerates Review of Ultra-Rare Barth Syndrome Drug – Wha…

YouTubeMedia Mindset

Mother Pleads for FDA to Approve Life-Saving Drug for Her Son In Washington, D.C., a mother is fighting for her son's life. He suffers from Barth Syndrome, an ultra-rare disease that leads to heart failure in young boys. His only lifeline is Elamipretide, a mitochondrial drug that has transformed his health. At just 20 days old, her son went into acute heart failure. Today, after 4 months on Elamipretide, his heart function has returned to near normal. The problem: the FDA has delayed approval f

Mother Pleads for FDA to Approve Life-Saving Drug for Her Son In W…

235 views5 days ago

FacebookLindellTV

Orland Park family campaigns for FDA to approve drug to treat Barth syndrome

Orland Park family campaigns for FDA to approve drug to treat Bart…

Microsoft NewsABC 7 Chicago

Desperate Fight for FDA Approval: Kids with Barth Syndrome Need H…

YouTubeMedia Mindset

FDA to Decide Soon on Stealth Bio's Elamipretide for Rare Barth Syndr…

1 views2 days ago

YouTubeNowCulture

Altimmune: FDA Fast Track Designation for Pemvidutide in Al…

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